Toddler doing well after receiving newest gene therapy available on NHS
25 Jun 2025, 9:23 a.m.
A toddler with a life-limiting and life-threatening rare disease is the youngest to be treated with the newest gene therapy available on the NHS at GOSH.
Genes may help to predict which children will respond well to arthritis treatment
16 Jun 2025, 4:37 p.m.
A team of researchers at Great Ormond Street Hospital (GOSH) and University College London (UCL) have identified a set of genes that could be used to help doctors predict which children will respond well to treatment for juvenile idiopathic arthritis.
GOSH and UCL have signed a landmark agreement to simplify the commercialisation of any joint research and innovation and ensure any financial proceeds are shared equally.
Patients and public help create multilingual resources for expectant parents
4 Jun 2025, 3:21 p.m.
A group of clinicians and researchers at GOSH have developed information about a test offered in pregnancy called prenatal sequencing in the UK’s 12 most common languages.