https://www.gosh.nhs.uk/our-research/our-research-infrastructure/nihr-great-ormond-street-hospital-brc/brc-news/?page=2

Biomedical Research Centre news

Boy with brown hair stood infront of a white car holding up a piece of paper driving license

Teenager off to university after life-changing gene therapy

18 Aug 2025, 6 a.m.

A teenager with a rare, life-limiting genetic condition is off to university after receiving a gene therapy that changed his life.

A boy stood in front of mountains wearing a black baseball cap and smiling.

Stem cell treatment can improve rare skin condition in children

15 Aug 2025, 9:46 a.m.

Children with a rare skin condition have found their symptoms have improved through taking part in the largest clinical trial of its kind, led by clinicians at Great Ormond Street Hospital for Children (GOSH).

Young people donate tissue samples to unlock mysteries of arthritis

2 Jul 2025, 9:49 a.m.

A new groundbreaking study led by researchers at the University of Birmingham, Great Ormond Street Hospital, University College London and Birmingham Children’s Hospital has revealed important clues into what is driving arthritis in children.

Toddler doing well after receiving newest gene therapy available on NHS

25 Jun 2025, 9:23 a.m.

A toddler with a life-limiting and life-threatening rare disease is the youngest to be treated with the newest gene therapy available on the NHS at GOSH.

Researcher holding a pipette dropping liquid into a test tube

Genes may help to predict which children will respond well to arthritis treatment

16 Jun 2025, 4:37 p.m.

A team of researchers at Great Ormond Street Hospital (GOSH) and University College London (UCL) have identified a set of genes that could be used to help doctors predict which children will respond well to treatment for juvenile idiopathic arthritis.