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Celebrating the Impact of the Professor Maria Bitner-Glindzicz Memory Fund

18 Nov 2025, 6 p.m.

The third annual report of the Maria Bitner-Glindzicz Memory Fund has just been compiled - The fund continues to support ground-breaking research and early career development.

Jacob sitting on sofa with his mum, dad and sister, in front of a navy blue wall

Mystery of treatment resistant childhood leukaemia uncovered

12 Nov 2025, 11:46 a.m.

Discovery of a new cancer cell type could enable testing to predict treatment-resistant blood cancer in children with a certain type of leukaemia.

Groundbreaking study highlights potential retinal marker that could identify sensory traits linked to autism

13 Nov 2025, 3 p.m.

A groundbreaking study led by researchers at Great Ormond Street Hospital and University College London published in Scientific Reports has found a significant link between altered retinal function and motion perception deficits in autism spectrum d…

Four members of staff standing in ZCR atrium in front of windows that look over labs

GOSH manufactures new gene therapy for rare condition

24 Nov 2025, 10:40 a.m.

A specialist laboratory team based at Great Ormond Street Hospital have manufactured a new gene therapy to treat a baby with the rare genetic condition, Hunter Syndrome.

A family smile at the camera with a stadium roof in the background. They are all smiling and laughing and the boy at the back is wearing novelty glasses

‘Ready-made’ T-cell gene therapy tackles ‘incurable’ T-Cell leukaemia

8 Dec 2025, 9:33 p.m.

A groundbreaking new treatment using gene-edited immune cells, developed at GOSH and UCL has shown promising results in helping children and adults fight a rare and aggressive cancer

Four people wearing lab coats using lab equipment

New consortium aims to help improve care for arthritis patients

19 Dec 2025, 10:23 a.m.

A new UK-led research group, including Great Ormond Street Hospital and University College London, aims to improve the lives of children, young people and adults with arthritis by defining for the first time what being in ‘remission’ from arthritis truly

Four researchers wearing lab coats in a line, with the staff member at the front holding a pipette

NIHR launches £13.7m investment into brain tumour research

19 Dec 2025, 11:47 a.m.

The National Institute for Health and Care Research (NIHR) has announced a £13.7 million investment that will support ground-breaking research to develop novel brain tumour treatments in the UK.

Will sitting on the front of HMS Belfast on the river Thames

Lab-grown mini-stomachs could boost understanding of rare diseases

26 Jan 2026, 1:03 p.m.

Researchers at Great Ormond Street Hospital (GOSH) and University College London (UCL) have developed the first-ever lab-grown mini-stomach that contains the key components of the full-sized human organ.

Unidentified person cutting out letters for an arts project, May 2017

Good Hope Works at GOSH

17 May 2017, 12:53 p.m.

Good Hope Works is an exciting creative research project facilitated by GOSH Arts and undertaken by artist Joanna Brinton. The project has engaged staff from across Great Ormond Street Hospital (GOSH) and will culminate in the installation of a permanent

£1 million award to push forward regenerative medicine research

13 Dec 2018, 10:19 a.m.

Researchers at Great Ormond Street Hospital (GOSH) and the UCL Great Ormond Street Institute of Child Health (ICH) are to lead a new collaboration exploring how stem cells can be engineered to evade immune responses.

AI bodysuit trial launched to help treat Duchenne muscular dystrophy

1 Feb 2018, 11:57 a.m.

A new artificially intelligent bodysuit to help understand how mobility is affected in boys with Duchenne will be trialled in a collaboration between researchers at Great Ormond Street Hospital (GOSH) and Imperial College London.

A liquid handling robot appears placing ampules into laboratory trays.

BRC researchers part of collaboration to improve efficiency of gene therapy products

26 Jul 2018, 3:56 p.m.

A new collaboration aiming to develop advanced technologies for manufacturing ex vivo gene therapy products has been established between researchers at UCL Great Ormond Street Institute of Child Health (ICH) and Plasticell, a developer of stem cell techno

Meredyth Wilkinson, one of the study's first authors

Cutting edge new method reveals novel cause of Juvenile dermatomyositis

25 Jun 2018, 10:18 a.m.

A new in-depth method has helped shed light on the key role of B cells, a type of immune cell, in the rare childhood condition Juvenile dermatomyositis (JDM).

Driving forward medical device development

2 Oct 2019, 4:57 p.m.

The NIHR GOSH BRC last month hosted an inaugural medical devices workshop, in partnership with the UCL Institute of Healthcare Engineering.

Drug for Duchenne Muscular Dystrophy shows promise in clinical trial

21 Aug 2017, 12:02 p.m.

An international clinical trial has found that the drug ataluren can improve mobility for children with a severe form of Duchenne muscular dystrophy (DMD).

Film celebrates success of Biomedical Research Centres set up by outgoing UK Chief Medical Officer

14 Oct 2019, 11:37 a.m.

NHS patients who have taken part in clinical trials have expressed their gratitude to researchers in a film celebrating the work of the National Institute for Health Research (NIHR) Biomedical Research Centres (BRCs), including GOSH BRC, to mark the retir

First children have gene therapy treatment for blindness at GOSH

18 Feb 2020, 5:33 p.m.

The first paediatric patients have received a pioneering new gene therapy that can restore eyesight at Great Ormond Street Hospital.

Phoebe and Fenella took part in a clinical trial at GOSH

First drug to reduce fever flares in children with recurrent fever conditions

17 Aug 2018, 12:02 p.m.

Injections of the drug canakinumab significantly reduced the number of fever episodes in children with three different types of recurrent fever conditions, in an international trial led at GOSH by Professor Paul Brogan.

Test tubes on a revolving plate in a lab

Funding boost to develop novel therapy for rare metabolic condition

1 Apr 2019, 10:19 a.m.

GOSH and UCL Great Ormond Street Institute of Child Health (ICH) researchers Professor Paul Gissen and Dr Julien Baruteau will be part of a new collaboration with Evox Therapeutics that aims to develop a new therapy for the life threatening metabolic cond

Gene therapy treatment manufactured at GOSH and ICH used to treat world's first patient with life limiting genetic condition, MPSIIIA

28 May 2019, noon

A two-year old patient at the Royal Manchester Children’s Hospital (RMCH) is the first in the world to receive a pioneering new gene therapy treatment for the rare and life-limiting genetic condition, Mucopolysaccharidosis IIIA (MPSIIIA). The treatment wa

Celebrating the Impact of the Professor Maria Bitner-Glindzicz Memory Fund

Mystery of treatment resistant childhood leukaemia uncovered

Groundbreaking study highlights potential retinal marker that could identify sensory traits linked to autism

GOSH manufactures new gene therapy for rare condition

‘Ready-made’ T-cell gene therapy tackles ‘incurable’ T-Cell leukaemia

New consortium aims to help improve care for arthritis patients

NIHR launches £13.7m investment into brain tumour research

Lab-grown mini-stomachs could boost understanding of rare diseases

Good Hope Works at GOSH

£1 million award to push forward regenerative medicine research

AI bodysuit trial launched to help treat Duchenne muscular dystrophy

BRC researchers part of collaboration to improve efficiency of gene therapy products

Cutting edge new method reveals novel cause of Juvenile dermatomyositis

Driving forward medical device development

​Drug for Duchenne Muscular Dystrophy shows promise in clinical trial

Film celebrates success of Biomedical Research Centres set up by outgoing UK Chief Medical Officer

First children have gene therapy treatment for blindness at GOSH

First drug to reduce fever flares in children with recurrent fever conditions

Funding boost to develop novel therapy for rare metabolic condition

Gene therapy treatment manufactured at GOSH and ICH used to treat world's first patient with life limiting genetic condition, MPSIIIA

Drug for Duchenne Muscular Dystrophy shows promise in clinical trial