UK’s first gene therapy baby celebrates 21st birthday
1 Oct 2021, 11 a.m.
The first child to be treated in the UK with gene therapy celebrates his 21st birthday this week, twenty years after having the pioneering treatment at Great Ormond Street Hospital for Children (GOSH).
Pfeiffer syndrome is a type of complex craniosynostosis. There are three different types of Pfeiffer syndrome: Types 1, 2 and 3 (which also known as cloverleaf skull). This page from Great Ormond Street Hospital (GOSH) explains the causes, symptoms and tr
GOSH to provide support for AI and Machine Learning as part of new paediatric HealthTech Research Centre
23 Nov 2023, 10 a.m.
GOSH will support the new Child and Young People’s HealthTech Research Centre (HRC), led by Sheffield Children’s Hospital, as leads for AI and Machine Learning.
Celebrating 25 years of saving children’s lives with gene therapy
23 Jul 2026, 11:43 a.m.
Marking 25 years since delivering the first ground-breaking gene therapy here at GOSH, having now treated more than 135 children with rare and life-threatening conditions across the world.
CLOSED: Our NIHR Great Ormond Street Biomedical Research Centre is delighted to open the first call for applications for a Research Communications Internship for existing staff of GOSH or UCL GOS ICH, specialising in social media.
Great Ormond Street Hospital's International Observership Programme offers international clinicians a unique opportunity to observe healthcare experts in a world-renowned paediatric setting. This programme is designed to support global colleagues in…
Looking after your child's skin during a hospital stay
This page explains about looking after your child's skin during a hospital stay and what to expect when your child comes to Great Ormond Street Hospital (GOSH).
Open tip rhinoplasty for children with craniofacial disorders
The bridge of the nose is made of bone but the rest of the nose is a flexible tissue called cartilage. A rhinoplasty is an operation to reshape the bone and cartilage in the nose. An open tip rhinoplasty is one where incisions are made to access inside th
Corticosteroids for children with neuromuscular disorders
This information has been provided to help answer some of the questions you may have about steroid medication for children with neuromuscular disorders.
Toddler doing well after receiving newest gene therapy available on NHS
25 Jun 2025, 9:23 a.m.
A toddler with a life-limiting and life-threatening rare disease is the youngest to be treated with the newest gene therapy available on the NHS at GOSH.
Multiple sclerosis (MS) is a common neurological condition affecting around 100,000 adults in the UK, but it is rare in childhood – and particularly rare in children under 12. Specialist care for these children and young people is therefore crucial and Gr
Back for 2026: NIHR GOSH BRC Research Communications Internship
OPEN: Our NIHR Great Ormond Street Biomedical Research Centre is delighted to open the 2026 call for applications for a Research Communications Internship for existing staff of UCL GOS ICH
NIHR GOSH BRC Research Communications Internship 2023
CLOSED: Our NIHR Great Ormond Street Biomedical Research Centre is delighted to open the first call for applications for a Research Communications Internship for existing staff of GOSH or UCL GOS ICH, specialising in social media.
Children are incredibly active and they have little sense of danger so it is not surprising that they are prone to head injuries. In addition, their heads are large in proportion to their bodies and therefore more vulnerable to damage than adult heads. Th
Monobloc advancement with or without using a rigid external distraction (RED) frame
Monobloc advancement is an operation to reshape the front portion of the skull and face including the upper jaw to correct an abnormal head shape. This page from Great Ormond Street Hospital (GOSH) explains about the operation called monobloc advancement
This information from Great Ormond Street Hospital (GOSH) explains about medicines used to treat children and young people with neuropathic pain – pain caused by the nerves sending wrong signals to and from the brain. At GOSH, we mainly use amitriptyline
In this theme we will build our capacity to offer clinical trial options to children affected by rare and complex conditions who have limited treatment options. To do this we will invest in more staff who are trained to deliver specialist treatments…
Intramedullary rodding surgery for children with Osteogenesis Imperfecta (OI)
Children and young people with Osteogenesis Imperfecta (OI) are more likely to develop fractures and bony changes such as bowing (bending) and shortening. Rodding surgery may be suggested or recommended by your child’s medical team. This page from Great O
