BRC news

Researchers at the UCL Great Ormond Street Institute of Child Health (ICH) and Great Ormond Street Hospital (GOSH) are to lead a new clinical trial for Kawasaki syndrome (KD-CAAP), a rare immune system condition that causes swelling of the blood vessels of the heart and can lead to severe fever and risk of heart problems such as aneurysms.

A two-year old patient at the Royal Manchester Children’s Hospital (RMCH) is the first in the world to receive a pioneering new gene therapy treatment for the rare and life-limiting genetic condition, Mucopolysaccharidosis IIIA (MPSIIIA). The treatment was manufactured at Great Ormond Street Hospital (GOSH) and the UCL Great Ormond Street Institute of Child Health (ICH) after being developed by RMCH and the University of Manchester.

An advanced new method for generating stem cells quickly and efficiently has been developed by an international team of researchers.

A team from University College London Hospitals (UCLH), UCL and Great Ormond Street Hospital (GOSH) has won the clinical leadership team award in the BMJ awards, the UK's leading medical awards which promote excellence in healthcare and recognise the inspirational work of healthcare teams across the country.

Over 150 people came along to the National Institute for Health Research (NIHR) GOSH Biomedical Research Centre showcase last month to hear about our latest research highlights - from cutting edge CAR-T therapies for leukaemia, to Oculome genomic sequencing to diagnose rare childhood eye conditions.

GOSH and UCL Great Ormond Street Institute of Child Health (ICH) researchers Professor Paul Gissen and Dr Julien Baruteau will be part of a new collaboration with Evox Therapeutics that aims to develop a new therapy for the life threatening metabolic condition, argininosuccinic aciduria (ASA)

A cutting-edge research project applying the next generation of genome editing to treat aggressive childhood leukaemia has received over £1.4 million of funding from UK Research and Innovation.

Over 30 nurses and allied health professionals (AHPs) attended a training weekend hosted by GOSH’s Centre for Outcomes and Experience Research in Children’s Health Illness and Disability (ORCHID) earlier this month.