BRC news

BRC latest news

This displays the latest news items related to the Biomedical Research Centre.

My path to research: Meet GOSH physiotherapist Lesley

Meet physiotherapist Lesley Katchburian who cares for Cora in episode four of Paul O’Grady’s Little Heroes. Lesley, who is Lead Clinical Specialist Physiotherapist for Botulinum Toxin Services in Neurodisability at GOSH, explains why botulinum toxin can be helpful for children with cerebral palsy and why research is so important. 

Novel therapy for Battens Disease available on the NHS

Patients at Great Ormond Street Hospital (GOSH) and across England are set to receive treatment for the rare nervous system condition Battens Disease, following a deal between the NHS and manufacturer Biomarin. The drug, which is called cerliponase alfa or Brineura, has been approved by the NHS following successful clinical trials at GOSH in collaboration with other centres from across the world. 

How 3d modelling and virtual reality can benefit patients and staff ahead of surgery

​Joe, aged 15, who features on Paul O’Grady’s Little Heroes, is being treated at GOSH for Marfan Syndrome, a genetic disorder that affects the body’s connective tissue, which plays an important role in helping the body grow and develop properly. Joe has an associated heart condition and required surgery to replace his aorta, the body’s main artery. 

The medical and research team involved in his care share how they have used pioneering 3D Heart Modelling and Virtual Reality to aid understanding of his heart condition ahead of surgery. 

New CAR T-cell therapy for leukaemia associated with less dangerous side effects

A clinical trial to investigate a novel CAR T-cell therapy, designed to target cancer cells more quickly and cause less side effects, has shown very promising results for children with previously incurable acute lymphoblastic leukaemia (ALL).