https://www.gosh.nhs.uk/our-research/our-research-infrastructure/nihr-great-ormond-street-hospital-brc/brc-news/?page=34

Biomedical Research Centre news

Researchers unlock new treatment options for babies with brain tumours

3 Apr 2020, 12:05 p.m.

An international collaboration including researchers from the UCL Great Ormond Street Institute of Child Health (ICH) has found brain tumours in babies are biologically different to those in older children and could be targeted by existing medications.

New gene therapy shows promise for life-threatening blood disorder X-CGD

9 Mar 2020, 3:29 p.m.

A new gene therapy developed by researchers at Great Ormond Street Hospital (GOSH) has been used to treat patients with a rare disease called X-linked chronic granulomatous disease (X-CGD), as part of an international study.

Meet the GOSH brain tumour trials team

9 Mar 2020, 10:24 a.m.

Diagnosis with a brain tumour can bring family life to a standstill in the worst possible way. But it also sparks an immediate flurry of activity, as a multi-disciplinary GOSH team springs into action around the child and their family. From radiology and

GOSH research brings Duchenne muscular dystrophy drug one step closer to UK patients

5 Mar 2020, 9:30 p.m.

A drug that ‘skips over’ a genetic fault responsible for the fatal muscle-wasting condition Duchenne muscular dystrophy (DMD) has shown promising results in an international trial led by Great Ormond Street Hospital (GOSH).

Marking Rare Disease Day at GOSH: DNA keyrings and family trees

4 Mar 2020, 1:28 p.m.

For this year's Rare Disease Day on 29th February, we invited children and young people at GOSH to make their own DNA keyring, map out their family tree, learn more about the genetics of rare diseases and even get a 'rare' new look.