https://www.gosh.nhs.uk/our-research/our-research-infrastructure/nihr-great-ormond-street-hospital-brc/brc-news/?page=26

Biomedical Research Centre news

Gene therapy offers hope to children with rare and fatal brain diseases

29 Jun 2021, 10 a.m.

Scientists and doctors at UCL GOS ICH and GOSH have given hope of a gene therapy cure to children with a rare degenerative brain disorder called Dopamine Transporter Deficiency Syndrome (DTDS)

Origins of kidney cancers confirmed

23 Jun 2021, 10 a.m.

The origins of seven types of kidney cancer, including several rare subtypes, have been identified.

Helping parents find answers after miscarriage

21 Jun 2021, 11:22 a.m.

A team at GOSH have developed a non-invasive imaging technique for the post-mortem imaging of babies who are miscarried or stillborn.

New insight into when CAR T is effective against childhood leukaemia

24 May 2021, 4 p.m.

Scientists studying the effectiveness of CAR T-cell therapies in children with leukaemia have discovered a small sub-set of T-cells that are likely to play a key role in whether the treatment is successful

International study finds gene therapy offers a potential cure to children born without an immune system

11 May 2021, 11:31 a.m.

An international team of researchers at GOSH and UCLA have developed a gene therapy that successfully treated 48 out of 50 children with a form of severe combined immunodeficiency