Cannabidiol trial shows reduction in seizures for children with Dravet syndrome
30 May 2017, 12:58 p.m.
A trial conducted in Europe and the USA has shown that cannabidiol – a drug derived from cannabis but with the psycho-active elements removed – reduces seizures in children with a form of drug resistant epilepsy, known as Dravet syndrome.
Molecular diagnoses of century-old childhood tumours reveals cancer causing mutations
24 May 2017, 2:29 p.m.
A collection of 100-year old tumour samples held at Great Ormond Street Hospital (GOSH) has helped pinpoint the genetic mutations that cause some of the rarest childhood cancers.
A team led by Professor Paolo De Coppi has announced that they are set to build and transplant an oesophagus using organs harvested from pigs and then modified using a child’s stem cells. The organs will be created for children who are born with a severe
Researchers awarded up to £1 million to develop gene therapy for serious immunodeficiency
24 Apr 2017, 11:35 a.m.
The UCL Technology Fund (UCLTF) has approved an investment of up to £1 million to support researchers Professor Adrian Thrasher, Professor Bobby Gaspar, and Dr GiorgiaSantilli in developing a gene therapy approach for treating p47phox-deficient chronic gr
Tissue removed during heart surgery is saving lives of children with no immune system
15 Apr 2017, 2:31 p.m.
In a European first, a little-known gland called the ‘thymus’, some of which is routinely removed during cardiac surgery, has saved the lives of children with a life threatening immunodeficiency condition, complete DiGeorge syndrome (cDGS).