Research and Innovation

BRC researchers part of collaboration to improve efficiency of gene therapy products

A new collaboration aiming to develop advanced technologies for manufacturing ex vivo gene therapy products has been established between researchers at UCL Great Ormond Street Institute of Child Health (ICH) and Plasticell, a developer of stem cell technologies.

New funding to support pioneering thymus transplant research at GOSH

Professors Graham Davies and Adrian Thrasher have been awarded funding from Great Ormond Street Hospital (GOSH) Charity to further develop a cutting-edge new treatment for children with the rare immunodeficiency condition complete DiGeorge syndrome (cDGS).

Precision medicine improves growth for children with a rare form of rickets

A new, targeted drug has been shown to significantly improve growth and control of rickets in children with X-linked hypophosphataemic rickets (XLH), a serious condition affecting about 300 children in the UK.

XLH is caused by genetic mutation that leads to excess activity of fibroblast...

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