Professors Bobby Gasper and Adrian Thrasher, both members of the BRC senior management team, have been awarded the UCL Business Award, in recognition of their work on the spin-out company Orchard Therapeutics.
GOSH Biomedical Research Centre researcher Dr John Counsell has been awarded up to £75,000 of funding from the UCL Therapeutic Acceleration Support (TAS) Fund for a study exploring the use of novel vectors in gene therapy for Duchenne Muscular Dystrophy (DMD).
A drug for Duchenne Muscular Dystrophy (DMD), originally developed by BRC Theme Lead Professor Francesco Muntoni’s Consortium in the UK, has been filed by Sarepta Therapeutics for accelerated approval by the United States Food and Drug Adminstration (FDA).
GOSH Arts and ORCHID (Centre for Outcomes and Experience Research in Children’s Health, Illness and Disability) have worked with patients, artists and health creatives to develop Blood Quest, an app that helps inform, entertain and distract children before and during their blood tests.
The prospect of widespread access to a life-changing drug for children with a rare muscular disorder is a step closer today after the United States Food and Drug Administration (FDA) granted accelerated approval for a new medication.
Hundreds of children have been trained today as young lifesavers at Great Ormond Street Hospital (GOSH), learning vital cardiopulmonary resuscitation (CPR) skills as part of the national Restart A Heart Day.
To launch Creativity and Wellbeing Week (12-18 June 2017), the London Arts in Health Forum (LAHF) and GOSH Arts brought together artists, curators, researchers and museum experts at Great Ormond Street Hospital (GOSH).
A trial conducted in Europe and the USA has shown that cannabidiol – a drug derived from cannabis but with the psycho-active elements removed – reduces seizures in children with a form of drug resistant epilepsy, known as Dravet syndrome.